Gene therapy success story -
https://www.bloomberg.com/news/articles/2019-04-17/-bubble-boys-cured-in-medical-breakthrough-using-gene-therapy
"'In a major scientific breakthrough, researchers at St. Jude Children’s Research Hospital in Memphis have developed a one-time, personalized treatment used to correct the genetic defect and build fully functioning immune systems in infants with the condition, formally known as X-linked severe combined immunodeficiency, or SCID. "'